TY  - JOUR
AU  - Phillips, Jonathan E.
AU  - Gomer, Richard H.
PY  - 2016
TI  - A canine model for neuronal ceroid lipofuscinosis highlights the promise of gene therapy for lysosomal storage diseases
JF  - Annals of Translational Medicine; Vol 4, Supplement 1 (October 31, 2016): Annals of Translational Medicine
Y2  - 2016
KW  - 
N2  - Patients with lysosomal storage diseases (LSDs) have abnormal lysosomal accumulation of waste products, due in most cases to enzyme deficiencies (1).
UR  - https://atm.amegroups.org/article/view/12212